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Publications by authors named "Adam Eliav"

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Gene therapy for guanidinoacetate methyltransferase deficiency restores cerebral and myocardial creatine while resolving behavioral abnormalities.
Suhail Khoja, Jenna Lambert, Matthew Nitzahn, Adam Eliav, YuChen Zhang

Mol Ther Methods Clin Dev· June 2022


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Intermittent lipid nanoparticle mRNA administration prevents cortical dysmyelination associated with arginase deficiency.
Suhail Khoja, Xiao-Bo Liu, Brian Truong, Matthew Nitzahn, Jenna Lambert, Adam Eliav

Mol Ther Nucleic Acids· June 2022


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CRISPR-Mediated Genomic Addition to CPS1 Deficient iPSCs is Insufficient to Restore Nitrogen Homeostasis.
Matthew Nitzahn, Brian Truong, Suhail Khoja, Agustin Vega-Crespo, Colleen Le, Adam Eliav

Yale J Biol Med· December 2021


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