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Publications by authors named "April Destefano"

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A compact base editor rescues AATD-associated liver and lung disease in mouse models.
Jenny Gao, Nathan Bamidele, Debora Pires-Ferreira, Chunwei Zheng, April Destefano

Mol Ther· November 2025


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A single amino acid variant in the variable region I of AAV capsid confers liver detargeting.
Ruxiao Xing, Mengyao Xu, Darcy Reil, April Destefano, Mengtian Cui

PLoS Pathog· September 2025


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A single amino acid variant in the variable region I of AAV capsid confers liver detargeting.
Ruxiao Xing, Mengyao Xu, Darcy Reil, April Destefano, Mengtian Cui

bioRxiv· June 2025


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A Compact Base Editor Rescues AATD-associated Liver and Lung Disease in Mouse Models.
Jenny Gao, Nathan Bamidele, Debora Pires-Ferreira, April Destefano, Qiushi Tang

bioRxiv· May 2025


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Primate archaeology.
Michael Haslam, Adriana Hernandez-Aguilar, Victoria Ling, Susana Carvalho, Ignacio de la Torre, April DeStefano

Nature· July 2009


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