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Publications by authors named "Chiara Filisetti"

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Non-neurological, non-skeletal outcomes after hematopoietic stem and progenitor cell-gene therapy (OTL-203) for Hurler syndrome.
Francesca Tucci, M Luz Uria Oficialdegui, Giulia Consiglieri, Matilde Cossutta, Chiara Filisetti

Mol Ther· January 2026


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Ultrasonographic hip morphology in mucopolysaccharidosis type I Hurler after hematopoietic stem cell gene therapy.
Maurizio De Pellegrin, Chiara Filisetti, Matilde Cossutta, Michele Colombo, Giulia Consiglieri

J Child Orthop· October 2025


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Early skeletal outcomes after hematopoietic stem and progenitor cell gene therapy for Hurler syndrome.
Giulia Consiglieri, Francesca Tucci, Maurizio De Pellegrin, Barbara Guerrini, Alessandro Cattoni, Chiara Filisetti

Sci Transl Med· May 2024


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Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome.
Bernhard Gentner, Francesca Tucci, Stefania Galimberti, Francesca Fumagalli, Maurizio De Pellegrin, Chiara Filisetti

N Engl J Med· November 2021


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