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Publications by authors named "Elise B Diffie"

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Clinical and biochemical abnormalities in a feline model of GM2 activator deficiency.
Sidney J Beecy, Amanda L Gross, Anne S Maguire, Leah M K Hoffman, Elise B Diffie

Mol Genet Metab· January 2025


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7T MRI Predicts Amelioration of Neurodegeneration in the Brain after AAV Gene Therapy.
Heather L Gray-Edwards, Anne S Maguire, Nouha Salibi, Lauren E Ellis, Taylor L Voss, Elise B Diffie

Mol Ther Methods Clin Dev· June 2020


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A Safe and Reliable Technique for CNS Delivery of AAV Vectors in the Cisterna Magna.
Toloo Taghian, Miklos G Marosfoi, Ajit S Puri, Oguz I Cataltepe, Robert M King, Elise B Diffie

Mol Ther· February 2020


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