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Publications by authors named "Eva Stumpe"

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Delphi consensus on gene therapy of spinal muscular atrophy with onasemnogene abeparvovec in Germany, Austria and Switzerland-part I-systematic literature review and existing evidence.
Claudia Weiß, Katharina Vill, Matthias Baumann, Günther Bernert, Astrid Blaschek, Eva Stumpe

J Neuromuscul Dis· November 2025


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Thorsten Langer, Nicole Gusset, Astrid Pechmann, Eva Stumpe, Susanne Dürr

Z Evid Fortbild Qual Gesundhwes· September 2022


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Understanding European patient expectations towards current therapeutic development in spinal muscular atrophy.
Nicole Gusset, Caroline Stalens, Eva Stumpe, Lori Klouvi, Alexandre Mejat

Neuromuscul Disord· May 2021


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A Decision for Life - Treatment decisions in newly diagnosed families with spinal muscular atrophy (SMA).
Nicole Gusset, Yasemin Erbas, Olga Germanenko, Kacper Rucinski, Eva Stumpe

Eur J Paediatr Neurol· January 2021


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