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Publications by authors named "Giulia Forotti"

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Targeted antisense oligonucleotide treatment rescues developmental alterations in spinal muscular atrophy organoids.
Irene Faravelli, Paola Rinchetti, Monica Tambalo, Illia Simutin, Lisa Mapelli, Giulia Forotti

Nat Commun· December 2025


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CSF transplantation of a specific iPSC-derived neural stem cell subpopulation ameliorates the disease phenotype in a mouse model of spinal muscular atrophy with respiratory distress type 1.
Giulia Forotti, Monica Nizzardo, Monica Bucchia, Agnese Ramirez, Elena Trombetta

Exp Neurol· November 2019


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