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Publications by authors named "Max E Stern"

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AAV2-mediated intravitreal delivery of exon-specific U1 snRNA rescues optic neuropathy in a mouse model of familial dysautonomia.
Anil Chekuri, Krishnakanth Kondabolu, Emily G Kirchner, Swanand Koli, Matthew Chagnon, Max E Stern

bioRxivยท August 2025


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