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Publications by authors named "Nikki Cornell"

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Expressive language and social communication abilities in children with spinal muscular atrophy type 1.
Chiara Brusa, Bianca Buchignani, Chiara Cutri, Giorgia Coratti, Elaine Clark, Nikki Cornell

Dev Med Child Neurol· September 2025


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Profiling neuroinflammatory markers and response to nusinersen in paediatric spinal muscular atrophy.
Qiang Zhang, Ying Hong, Chiara Brusa, Mariacristina Scoto, Nikki Cornell

Sci Rep· October 2024


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Risdiplam in Spinal Muscular Atrophy: Safety Profile and Use Through The Early Access to Medicine Scheme for the Paediatric Cohort in Great Britain.
Nikki Cornell, Anne-Marie Childs, Elizabeth Wraige, Pinki Munot, Gautam Ambegaonkar

J Neuromuscul Dis· March 2024


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Variation in Transfusion Requirements Among Children With Thalassemia on Regular Transfusion Programs: Which Formula Closely Predicts the Actual Requirements?
Nikki Cornell, Michael Eisenhut, Stalin Ramprakash

J Pediatr Hematol Oncol· October 2017


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