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Publications by authors named "Nolan Tual"

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Successful treatment of severe MSUD in Bckdhb mice with neonatal AAV gene therapy.
Clément Pontoizeau, Clovis Gaborit, Nolan Tual, Marcelo Simon-Sola, Irina Rotaru

J Inherit Metab Dis· January 2024


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Neonatal gene therapy achieves sustained disease rescue of maple syrup urine disease in mice.
Clément Pontoizeau, Marcelo Simon-Sola, Clovis Gaborit, Vincent Nguyen, Irina Rotaru, Nolan Tual

Nat Commun· June 2022


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