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Publications by authors named "Somdatta Ray"

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Preclinical use of a clinically-relevant scAAV9/SUMF1 vector for the treatment of multiple sulfatase deficiency.
Maximiliano Presa, Rachel M Bailey, Somdatta Ray, Lauren Bailey, Saurabh Tata, Steven J Gray

Commun Med (Lond)· January 2025


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Bone marrow transplantation increases sulfatase activity in somatic tissues in a multiple sulfatase deficiency mouse model.
Maximiliano Presa, Vi Pham, Somdatta Ray, Pierre-Alexandre Piec, Jennifer Ryan

Commun Med (Lond)· October 2024


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New mouse models with hypomorphic SUMF1 variants mimic attenuated forms of multiple sulfatase deficiency.
Nicolina Cristina Sorrentino, Maximiliano Presa, Sergio Attanasio, Vincenzo Cacace, Martina Sofia, Somdatta Ray

J Inherit Metab Dis· March 2023


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