This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMolecMed We talk a lot about patient-led research foundations and clinical trial readiness because it matters a lot to us
Gene therapies for neurogenetic disorders.
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Feb 2025 – Nov 2025Where it's discussed
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X / Twitter15 posts
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Bluesky3 posts
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YouTube3 videos
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Facebook2 posts
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News2 articles
AI synopsis
What people are saying
The posts show high engagement and interest, with phrases like 'so fun to write' and mentions of 'transformative potential,' highlighting excitement. Supportive comments about the review and focus on patient foundations reflect agreement, whereas the moderate impact score suggests discussions center on ongoing research rather than immediate clinical breakthroughs.
Most posts express support and enthusiasm for the review, indicating agreement with its significance.
Posts demonstrate high interest through mentions of new developments, podcasts, and discussions around gene therapies.
Users actively engage by sharing links, discussing patient involvement, and emphasizing the importance of research foundations.
While the enthusiasm is clear, the actual perceived impact on clinical practice appears moderate, as most focus on research and awareness.
Abstract in brief
- Gene therapies for neurogenetic disorders target genetic mutations causing over 1700 different diseases, but delivery challenges like the blood-brain barrier and neuron postmitotic nature make treatment difficult.
- Since the approval of nusinersen in 2016, advancements have included new delivery methods such as BBB-crossing capsids, viral-like proteins, and lipid nanoparticles, as well as innovative therapeutic strategies like gene editing, RNA-based therapies, and epigenetics.
- Patient-led organizations have played a crucial role in speeding up research and trial readiness, helping shape the development of new treatment options and shaping the future of gene therapy for neurogenetic disorders.]
Top posts
Most liked on X and BlueskyCheck out our "Gene therapies for neurogenetic disorders" review at @cp-trendsmolecmed.bsky.social So fun to write! We talk a lot about #RareDisease patient foundations and clinical trial readiness because it matters a lot to us
Episode 9 of our AI podcast series: Gene Therapies for Neurogenetic Disorders The AI podcast covers the new review from @epilepsia , @CNSdrughunter & team on gene therapies for neurogenetic disorders. AI Podcasts in Spanish, German and English: https://t.co/JuItWjNa3W https://t.co/wi5S3rAGKb
"Gene therapies for neurogenetic disorders" http://dlvr.it/TPHWjf Orrin Devinsky, @cnsdrughunter.bsky.social & colleagues @cp-trendsmolecmed.bsly.social #SfN2025
ONLINE NOW: Gene therapies for neurogenetic disorders https://t.co/Brr6AeMyKr https://t.co/5VsAEMWrtu
RT @CNSdrughunter: This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMole…
All mentions
Advancements in Gene Therapies for Neurogenetic Disorders
This video explores current progress and future directions in gene therapies targeting neurogenetic disorders, emphasizing delivery challenges, innovative methods, and the vital role of patient organizations in…
Advances in Gene Therapies for Neurogenetic Disorders
This video reviews recent developments in gene therapies targeting neurogenetic disorders, including innovative delivery methods and therapeutic strategies like gene editing and RNA-based treatments, while highlighting…
Advances in Gene Therapies for Neurogenetic Disorders
This video reviews the current state and future directions of gene therapies for neurogenetic disorders, highlighting innovative delivery methods and therapeutic strategies that address challenges like the blood-brain…
"Gene therapies for neurogenetic disorders" http://dlvr.it/TPHWjf Orrin Devinsky, @cnsdrughunter.bsky.social & colleagues @cp-trendsmolecmed.bsly.social #SfN2025
RT @CNSdrughunter: This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMole…
RT @CNSdrughunter: This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMole…
Gene therapies for neurogenetic disorders https://t.co/W61atlpHvn
RT @CNSdrughunter: This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMole…
RT @CNSdrughunter: This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMole…
RT @CNSdrughunter: This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMole…
RT @TrendsMolecMed: ONLINE NOW: Gene therapies for neurogenetic disorders https://t.co/Brr6AeMyKr https://t.co/5VsAEMWrtu
Episode 9 of our AI podcast series: Gene Therapies for Neurogenetic Disorders The AI podcast covers the new review from @epilepsia , @CNSdrughunter & team on gene therapies for neurogenetic disorders. AI Podcasts in Spanish, German and English: https://t.co/JuItWjNa3W https://t.co/wi5S3rAGKb
RT @CNSdrughunter: This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMole…
RT @TrendsMolecMed: ONLINE NOW: Gene therapies for neurogenetic disorders https://t.co/Brr6AeMyKr https://t.co/5VsAEMWrtu
ONLINE NOW: Gene therapies for neurogenetic disorders https://t.co/Brr6AeMyKr https://t.co/5VsAEMWrtu
RT @CNSdrughunter: This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMole…
Gene therapies for neurogenetic disorders www.sciencedirect.com/science/arti...
RT @CNSdrughunter: This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMole…
RT @CNSdrughunter: This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMole…
Check out our "Gene therapies for neurogenetic disorders" review at @cp-trendsmolecmed.bsky.social So fun to write! We talk a lot about #RareDisease patient foundations and clinical trial readiness because it matters a lot to us
This was such a great review to write! Check out our "Gene therapies for neurogenetic disorders" review at @TrendsMolecMed We talk a lot about patient-led research foundations and clinical trial readiness because it matters a lot to us