Publications by authors named "Mark A Kay"

Claim this Profile
S
Stereo-random oligonucleotides enable efficient recruitment of ADAR in vitro and in vivo.
Laura S Pfeiffer, Tobias Merkle, Paul Vogel, Inga Jarmoskaite, Jonathan M Geisinger, Mark A Kay

Nat Commun· October 2025

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
L
Low-level shRNA Cytotoxicity Can Contribute to MYC-induced Hepatocellular Carcinoma in Adult Mice.
Shelly Beer, David I Bellovin, Joyce S Lee, Kimberly Komatsubara, Lora S Wang, Mark A Kay

Mol Ther· June 2025

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
F
Functional analysis of tRNA-derived small translational regulation.
Dongjin Kim, Hak Kyun Kim, Mark A Kay

Methods Enzymol· May 2025

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
T
The deLIVERed promises of gene therapy: Past, present, and future of liver-directed gene therapy.
Francesco Puzzo, Mark A Kay

Mol Ther· May 2025

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
O
Operationalising a Haemophilia Gene Editing Lexicon for Practical Use.
William McKeown, Cedric Hermans, Carmen Unzu, Mark A Kay, Flora Peyvandi

Haemophilia· March 2025

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
G
Genome engineering with Cas9 and AAV repair templates generates frequent concatemeric insertions of viral vectors.
Fabian P Suchy, Daiki Karigane, Yusuke Nakauchi, Maimi Higuchi, Jinyu Zhang, Mark A Kay

Nat Biotechnol· February 2025

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
D
Development of a novel gene editing lexicon for hemophilia: methodology and results.
Craig M Kessler, Leonard A Valentino, Courtney D Thornburg, Carmen Unzu, Mark A Kay

Res Pract Thromb Haemost· February 2025

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
A
AAV-mediated genome editing is influenced by the formation of R-loops.
Francesco Puzzo, Magdalena P Crossley, Aranyak Goswami, Feijie Zhang, Katja Pekrun, Mark A Kay

Mol Ther· December 2024

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
R
Ruvkun and Ambros recognized for miRNAs.
Mark A Kay

Mol Ther Nucleic Acids· December 2024

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
A
A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results.
Cedric Hermans, Leonard A Valentino, Courtney D Thornburg, Carmen Unzu, Mark A Kay

Haemophilia· November 2024

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
C
Correlation of antigen expression with epigenetic modifications after rAAV delivery of a human factor IX variant in mice and rhesus macaques.
Katja Pekrun, Calvin J Stephens, Adriana Gonzalez-Sandoval, Aranyak Goswami, Feijie Zhang, Mark A Kay

Mol Ther· July 2024

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
A
AAV-mediated genome editing is influenced by the formation of R-loops.
Francesco Puzzo, Magdalena P Crossley, Aranyak Goswami, Feijie Zhang, Katja Pekrun, Mark A Kay

bioRxiv· May 2024

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
S
Selection of viral capsids and promoters affects the efficacy of rescue of -deficient cochlea.
Ksenia A Aaron, Katja Pekrun, Patrick J Atkinson, Sara E Billings, Julia M Abitbol, Mark A Kay

Mol Ther Methods Clin Dev· September 2023

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
A
A standardized ontology for naming tRNA-derived RNAs based on molecular origin.
Andrew D Holmes, Patricia P Chan, Qi Chen, Pavel Ivanov, Laurence Drouard, Mark A Kay

Nat Methods· May 2023

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
A
A strategy for high antibody expression with low anti-drug antibodies using AAV9 vectors.
Meredith E Davis-Gardner, Jesse A Weber, Jun Xie, Katja Pekrun, Eric A Alexander, Mark A Kay

Front Immunol· May 2023

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
T
The AAV capsid can influence the epigenetic marking of rAAV delivered episomal genomes in a species dependent manner.
Adriana Gonzalez-Sandoval, Katja Pekrun, Shinnosuke Tsuji, Feijie Zhang, King L Hung, Mark A Kay

Nat Commun· April 2023

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
A
Aptamer-programmable adeno-associated viral vectors as a novel platform for cell-specific gene transfer.
Francesco Puzzo, Chuanling Zhang, Bethany Powell Gray, Feijie Zhang, Bruce A Sullenger, Mark A Kay

Mol Ther Nucleic Acids· March 2023

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
S
Selection of rAAV vectors that cross the human blood-brain barrier and target the central nervous system using a transwell model.
Ren Song, Katja Pekrun, Themasap A Khan, Feijie Zhang, Sergiu P Paşca, Mark A Kay

Mol Ther Methods Clin Dev· December 2022

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
F
Fludarabine increases nuclease-free AAV- and CRISPR/Cas9-mediated homologous recombination in mice.
Shinnosuke Tsuji, Calvin J Stephens, Giulia Bortolussi, Feijie Zhang, Gabriele Baj, Mark A Kay

Nat Biotechnol· August 2022

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
E
Evaluating the state of the science for adeno-associated virus integration: An integrated perspective.
Denise E Sabatino, Frederic D Bushman, Randy J Chandler, Ronald G Crystal, Beverly L Davidson, Mark A Kay

Mol Ther· August 2022

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
P
Promoterless Gene Targeting Approach Combined to CRISPR/Cas9 Efficiently Corrects Hemophilia B Phenotype in Neonatal Mice.
Michela Lisjak, Alessia De Caneva, Thibaut Marais, Elena Barbon, Maria Grazia Biferi, Mark A Kay

Front Genome Ed· March 2022

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
S
Selective Microvascular Tissue Transfection Using Minicircle DNA for Systemic Delivery of Human Coagulation Factor IX in a Rat Model Using a Therapeutic Flap.
Peter A Than, Christopher R Davis, Robert C Rennert, Shane D Morrison, Michael W Findlay, Mark A Kay

Plast Reconstr Surg· January 2022

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
T
The 3'tsRNAs are aminoacylated: Implications for their biogenesis.
Ziwei Liu, Hak Kyun Kim, Jianpeng Xu, Yuqing Jing, Mark A Kay

PLoS Genet· July 2021

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
R
RNA structure probing reveals the structural basis of Dicer binding and cleavage.
Qing-Jun Luo, Jinsong Zhang, Pan Li, Qing Wang, Yue Zhang, Mark A Kay

Nat Commun· June 2021

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis
I
Improved Genome Editing through Inhibition of FANCM and Members of the BTR Dissolvase Complex.
Gustavo de Alencastro, Francesco Puzzo, Mara Pavel-Dinu, Feijie Zhang, Sirika Pillay, Mark A Kay

Mol Ther· March 2021

Social Media Activity not collected for this article yet.

Sign Up to Request Social Media Analysis